遺伝子治療市場 – 2032年までの世界予測

Gene Therapy Market - Global Forecast to 2032

遺伝子治療市場 - タイプ(遺伝子サイレンシング)、ベクター [ウイルス(レトロウイルス、AAV)、非ウイルス(オリゴヌクレオチド)]、遺伝子タイプ(受容体、サイトカイン)、治療領域(腫瘍学、神経学)、送達方法(生体内、体外)、RoA(静脈内) - 2032年までの世界予測
Gene Therapy Market by Type (Gene silencing), Vector (Viral (Retroviral, AAV), Non-viral (Oligonucleotide)), Gene Type (Receptors, Cytokine), Therapeutic Area (Oncology, Neurology), Delivery Method (In-Vivo, Ex-Vivo), RoA (IV) - Global Forecast to 2032

商品番号 : SMB-18735

出版社MarketsandMarkets
出版年月2025年2月
ページ数434
図表数720
価格タイプシングルユーザライセンス
価格USD 4,950
種別英文調査報告書

Report Overview

The global gene therapy market is projected to reach USD 36.55 billion by 2032 from USD 8.85 billion in 2024, at a CAGR of 19.4% during the forecast period of 2024 to 2032.

世界の遺伝子治療市場は、2024年から2032年の予測期間中にCAGR 19.4%で、2024年の88億5,000万米ドルから2032年までに365億5,000万米ドルに達すると予測されています。

The growth of the gene therapy market has been significantly driven by increasing R&D investment by key players for the development gene therapy drugs and growing approval of novel gene therapies. However, complex regulatory frameworks and ethical concerns regarding genetic modifications are restraining market growth.

遺伝子治療市場の成長は、遺伝子治療薬開発の主要企業による研究開発投資の増加と新しい遺伝子治療の承認の増加によって大きく推進されてきました。しかし、複雑な規制の枠組みと遺伝子組み換えに関する倫理的懸念が市場の成長を抑制しています。

遺伝子治療市場 - 2032年までの世界予測
gene-therapy-market-Overview

“The intravenous route segment accounted for the largest share by route of administration in 2023.”

Based on route of administration, the gene therapy market is segmented into intravenous route, subcutaneous route and other routes. The intravenous route segment accounted for the largest share of the gene therapy market in 2023. The larger share of this segment is mainly attributed to the number of gene therapy administered through intravenous route is due to factors such as the high effectiveness of intravenous administration and high penetration of intravenous gene therapy currently approved and marketed products among others.

“The US has continued to dominate the gene therapy market during the forecast period of 2024-2032.”

The US is the world’s largest biopharmaceutical market and a leader in biopharmaceutical research/investments. Driven by the growing patient population suffering from chronid disease, increasing biopharmaceuticals’ importance, and the necessity of safe and high-quality products in the healthcare sector, growing investments and funding in biomedical research by government bodies and pharmaceutical & biotechnology companies. Also, a strong established presence of several market players in the region is another key factor supporting market growth. These key companies include, Biogen Inc. (US), Alnylam Pharmaceuticals, Inc. (US), and Sarepta Therapeutics, Inc. (US).

The primary interviews conducted for this report can be categorized as follows:

  • By Respondent: Supply Side- 70% and Demand Side 30%
  • By Designation: Managers – 45%, CXO & Directors – 30%, and Executives – 25%
  • By Region: North America -40%, Europe -25%, Asia-Pacific -25%, Latin America -5% and Middle East & Africa- 5%

List of  key Companies Profiled in the Report:

Biogen Inc. (US), Novartis AG (Switzerland), Alnylam Pharmaceuticals, Inc. (US), Sarepta Therapeutics, Inc. (US), Jazz Pharmaceuticals Plc (Ireland), Ferring B.V. (Switzerland), Pfizer Inc. (US), Amgen, Inc. (US), Johnson & Johnson Services, Inc. (US), Daiichi Sankyo Company, Limited. (Japan), BioMarin Pharmaceutical Inc. (US), Kyowa Kirin Co., Ltd. (Japan), Nippon Shinyaku Co., Ltd. (Japan), PTC Therapeutics (US), UniQure NV (Netherlands), Juventas Cell Therapy Ltd. (China), CRISPR Therapeutics (Switzerland), bluebird bio, Inc. (US), Krystal Biotech, Inc. (US), Shanghai Sunway Biotech Co., Ltd. (China), JW (Cayman) Therapeutics Co. Ltd (China), IASO Biotechnology (China), CARsgen Therapeutics Holdings Limited (China), Adaptimmune (UK), Sibiono GeneTech Co. Ltd. (China), and Ultragenyx Pharmaceutical Inc. (US).

遺伝子治療市場 - 2032年までの世界予測 ecosystem
gene-therapy-market-Ecosystem

Research Coverage:

This research report categorizes the gene therapy market by Therapy Type (Gene Silencing Therapy, Cell Replacement Therapy, Gene Augmentation Therapy and Other Therapies)), by Vector (Viral Vectors (Retroviral Vector (Gamma retroviral vectors, Lentiviral Vectors) AAV Vectors, and Other Viral Vectors), Non-viral Vectors (Oligonucleotides and Other Non-viral Vectors)), by Gene Type (Deficiency, Receptors, Antigen, Cytokine, Tumor Suppressor, and Othe Genes), by Therapeutic Area (Neurology, Oncology, Hematology and Other Therapeutic Areas), by Delivery Method (In Vivo and Ex Vivo), by Route of Administration (Intravenous Route, Subcutaneous Route, and Other Routes), by End User (Hospitals, Specialty Centers, and Other End Users) and by region (North America, Europe, Asia Pacific, Latin America, Middle East and Africa). The scope of the report covers detailed information regarding the major factors, such as drivers, restraints, challenges, and opportunities, influencing the growth of the oral proteins and peptides market. A detailed analysis of the key industry players has been done to provide insights into their business overview, products, solutions, key strategies, collaborations, partnerships, and agreements. New approvals/launches, collaborations and acquisitions, and recent developments associated with the gene therapy market.

Key Benefits of Buying the Report:

The report will help market leaders/new entrants by providing them with the closest approximations of the revenue numbers for the overall gene therapy market and its subsegments. It will also help stakeholders better understand the competitive landscape and gain more insights to better position their business and make suitable go-to-market strategies. This report will enable stakeholders to understand the market’s pulse and provide them with information on the key market drivers, restraints, opportunities, and challenges.

The report provides insights on the following pointers:

  • Analysis of key drivers (Growing demand for curative therapies for genetic disorders, rare diseases, and specific types of cancer, Increasing investments in gene therapy research, Growing technological advancements, and Robust clinical trial pipeline for gene therapy), restraints (High cost of gene therapy products, Complex regulatory frameworks and ethical concerns regarding genetic modifications, and Limited manufacturing scalability), opportunities (Expansion into rare diseases and unmet needs, Increasing focus on precision medicine, and Advancements in gene therapy delivery technologies), and Challenges (Complex manufacturing process, Short shelf life and supply chain challenges, and Lack of reimbursement).
  • Product Development/Innovation: Detailed insights on upcoming technologies, research and development activities, and new product approvals/launches in the gene therapy market.
  • Market Development: Comprehensive information about lucrative markets – the report analyses the market across varied regions.
  • Market Diversification: Exhaustive information about new products, untapped geographies, recent developments, and investments in the gene therapy market
  • Competitive Assessment: In-depth assessment of market shares, growth strategies and product offerings of leading players. A detailed analysis of the key industry players has been done to provide insights into their key strategies, product launches/ approvals, pipeline analysis, acquisitions, partnerships, agreements, collaborations, other recent developments, investment and funding activities, brand/product comparative analysis, and vendor valuation and financial metrics of the gene therapy market.

Table of Contents

1               INTRODUCTION              41

1.1           STUDY OBJECTIVES       41

1.2           MARKET DEFINITION   41

1.3           STUDY SCOPE   42

1.3.1        MARKETS COVERED & REGIONAL SEGMENTATION                 42

1.3.2        INCLUSIONS & EXCLUSIONS       43

1.3.3        YEARS CONSIDERED      44

1.3.4        CURRENCY CONSIDERED            44

1.4           STAKEHOLDERS               44

1.5           SUMMARY OF CHANGES               45

2               RESEARCH METHODOLOGY       46

2.1           RESEARCH DATA              46

2.1.1        SECONDARY RESEARCH                47

2.1.1.1    Key data from secondary sources       48

2.1.2        PRIMARY RESEARCH       48

2.1.2.1    Insights of primary experts 50

2.2           MARKET SIZE ESTIMATION         51

2.2.1        GLOBAL MARKET ESTIMATION 51

2.2.2        SEGMENTAL MARKET SIZE ESTIMATION              53

2.3           MARKET GROWTH RATE PROJECTIONS                54

2.4           MARKET BREAKDOWN AND DATA TRIANGULATION                 56

2.5           RESEARCH ASSUMPTIONS           57

2.6           RESEARCH LIMITATIONS             58

2.7           RISK ANALYSIS  58

3               EXECUTIVE SUMMARY  59

4               PREMIUM INSIGHTS       64

4.1           GENE THERAPY MARKET OVERVIEW     64

4.2           NORTH AMERICA: GENE THERAPY MARKET, BY THERAPY TYPE & COUNTRY (2024)          65

4.3           GENE THERAPY MARKET SHARE, BY END USER, 2024 VS 2032        66

4.4           GENE THERAPY MARKET: GEOGRAPHIC GROWTH OPPORTUNITIES              66

5               MARKET OVERVIEW       67

5.1           INTRODUCTION              67

5.2           MARKET DYNAMICS       67

5.2.1        DRIVERS               68

5.2.1.1    Growing demand for curative therapies for genetic disorders, rare diseases, and cancers            68

5.2.1.2    Increasing investments in gene therapy research            70

5.2.1.3    Technological advancements              71

5.2.1.4    Robust clinical trial pipeline for gene therapy 72

5.2.2        RESTRAINTS      73

5.2.2.1    High cost of gene therapy products   73

5.2.2.2    Complex regulatory frameworks and ethical concerns regarding genetic modifications           73

5.2.2.3    Limited manufacturing scalability     74

5.2.3        OPPORTUNITIES              74

5.2.3.1    Expansion into rare diseases and unmet needs                74

5.2.3.2    Increasing focus on precision medicine            75

5.2.3.3    Advancements in gene therapy delivery technologies    76

5.2.4        CHALLENGES    76

5.2.4.1    Complex commercial manufacturing and scaling process                 76

5.2.4.2    Short shelf life and supply chain challenges     77

5.2.4.3    Lack of reimbursement        77

5.3           TECHNOLOGY ANALYSIS             78

5.3.1        KEY TECHNOLOGIES     78

5.3.1.1    CRISPR-Cas9        78

5.3.1.2    RNA interference 78

5.3.1.3    Viral vectors           78

5.3.2        COMPLEMENTARY TECHNOLOGIES       79

5.3.2.1    Stem cell therapy  79

5.3.2.2    Omics technologies              79

5.3.3        ADJACENT TECHNOLOGIES       79

5.3.3.1    Nanoparticles        79

5.4           VALUE CHAIN ANALYSIS               80

5.5           SUPPLY CHAIN ANALYSIS             81

5.5.1        PROMINENT COMPANIES            81

5.5.2        SMALL AND MEDIUM-SIZED ENTERPRISES          81

5.5.3        END USERS         81

5.5.4        INVESTORS, VENTURE CAPITALISTS, AND FUNDING BODIES 81

5.5.5        REGULATORY BODIES  81

5.6           ECOSYSTEM ANALYSIS  82

5.7           PATENT ANALYSIS          85

5.8           PIPELINE ANALYSIS        88

5.9           REGULATORY LANDSCAPE         89

5.9.1        REGULATORY BODIES, GOVERNMENT AGENCIES, AND OTHER ORGANIZATIONS, BY REGION   89

5.9.2        REGULATORY FRAMEWORK       91

5.9.3        REIMBURSEMENT SCENARIO     92

5.10         PRICING ANALYSIS          94

5.10.1      AVERAGE SELLING PRICE TREND, BY KEY PLAYER                 94

5.10.2      AVERAGE SELLING PRICE TREND, BY REGION   96

5.11         TRENDS/DISRUPTIONS IMPACTING CUSTOMERS’ BUSINESSES       98

5.12         KEY CONFERENCES & EVENTS, 2025–2026              99

5.13         PORTER’S FIVE FORCES ANALYSIS           100

5.13.1      THREAT OF NEW ENTRANTS      101

5.13.2      THREAT OF SUBSTITUTES          101

5.13.3      BARGAINING POWER OF SUPPLIERS       101

5.13.4      BARGAINING POWER OF BUYERS             102

5.13.5      INTENSITY OF COMPETITIVE RIVALRY 102

5.14         KEY STAKEHOLDERS & BUYING CRITERIA            102

5.14.1      KEY STAKEHOLDERS IN BUYING PROCESS           102

5.14.2      BUYING CRITERIA           104

5.15         INVESTMENT & FUNDING SCENARIO     105

5.16         IMPACT OF AI ON GENE THERAPY MARKET        106

6               GENE THERAPY MARKET, BY THERAPY TYPE     108

6.1           INTRODUCTION              109

6.2           GENE SILENCING THERAPY        109

6.2.1        FLEXIBILITY AND PRECISION OF GENE SILENCING THERAPIES TO SUPPORT GROWTH         109

6.3           CELL REPLACEMENT THERAPY 113

6.3.1        LONG-TERM EFFECT OF THERAPY TO SUPPORT GROWTH IN ADOPTION               113

6.4           GENE AUGMENTATION THERAPY            116

6.4.1        EFFECTIVENESS AGAINST MONOGENIC DISORDERS TO DRIVE MARKET 116

6.5           OTHER THERAPIES         120

7               GENE THERAPY MARKET, BY VECTOR   124

7.1           INTRODUCTION              125

7.2           VIRAL VECTORS                125

7.2.1        RETROVIRAL VECTORS 129

7.2.1.1    Advantages of retroviral vectors to support market growth                 129

7.2.1.2    Gamma-retroviral vectors   132

7.2.1.2.1 Availability of gamma-retroviral vectors to support market growth    132

7.2.1.3    Lentiviral vectors  135

7.2.1.3.1 North America to dominate lentiviral vectors market    135

7.2.2        AAV VECTORS   138

7.2.2.1    Focus of clinical pipeline on adeno-associated viral vectors to drive growth          138

7.2.3        OTHER VIRAL VECTORS                141

7.3           NON-VIRAL VECTORS    144

7.3.1        OLIGONUCLEOTIDE VECTORS 148

7.3.1.1    Oligonucleotides to account for largest share of non-viral vectors market    148

7.3.2        OTHER NON-VIRAL VECTORS    151

8               GENE THERAPY MARKET, BY GENE TYPE             154

8.1           INTRODUCTION              155

8.2           DEFICIENCY      155

8.2.1        TECHNOLOGICAL ADVANCEMENT IN GENE THERAPIES TO BOOST GROWTH      155

8.3           RECEPTOR          159

8.3.1        INCREASING DEMAND FOR DEVELOPING RECEPTOR-BASED GENE THERAPY TO SUPPORT MARKET GROWTH                 159

8.4           ANTIGEN             162

8.4.1        INCREASING DEMAND FOR TARGETED THERAPIES TO PROPEL GROWTH            162

8.5           CYTOKINE          165

8.5.1        RISING R&D TO SUPPORT MARKET GROWTH    165

8.6           TUMOR SUPPRESSOR    169

8.6.1        RISING PREVALENCE OF CANCER TO PROPEL MARKET GROWTH             169

8.7           OTHER GENES  172

9               GENE THERAPY MARKET, BY THERAPEUTIC AREA                 176

9.1           INTRODUCTION              177

9.2           NEUROLOGY     177

9.2.1        ENHANCED DELIVERY METHODS AND ADVANCEMENTS IN GENE EDITING TECHNOLOGIES TO BOOST MARKET GROWTH          177

9.3           ONCOLOGY        181

9.3.1        RISING BURDEN OF CANCER TO SUPPORT MARKET GROWTH             181

9.4           HEMATOLOGY 184

9.4.1        INCREASING PREVALENCE OF GENETIC BLOOD DISORDERS TO BOOST MARKET GROWTH          184

9.5           OTHER THERAPEUTIC AREAS    188

10            GENE THERAPY MARKET, BY DELIVERY METHOD                 191

10.1         INTRODUCTION              192

10.2         IN VIVO DELIVERY          192

10.2.1      IN VIVO DELIVERY METHOD TO ACCOUNT FOR LARGEST MARKET SHARE IN 2023             192

10.3         EX VIVO DELIVERY          196

10.3.1      GROWING FOCUS ON ONCOLOGY THERAPEUTICS TO SUPPORT MARKET GROWTH     196

11            GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION          200

11.1         INTRODUCTION              201

11.2         INTRAVENOUS ROUTE  201

11.2.1      HIGH EFFECTIVENESS AND LARGE SHARE OF INTRAVENOUS PRODUCTS TO SUPPORT MARKET GROWTH                 201

11.3         SUBCUTANEOUS ROUTE              205

11.3.1      DEVELOPMENT OF IMPROVED DELIVERY DEVICES TO SUPPORT MARKET GROWTH     205

11.4         OTHER ROUTES                208

12            GENE THERAPY MARKET, BY END USER                212

12.1         INTRODUCTION              213

12.2         HOSPITALS         213

12.2.1      GROWING DEMAND FOR ADVANCED THERAPIES TO BOOST MARKET               213

12.3         SPECIALTY CENTERS     217

12.3.1      ADVANCEMENTS IN GENE THERAPY TECHNOLOGIES TO SUPPORT MARKET GROWTH              217

12.4         OTHER END USERS         220

13            GENE THERAPY MARKET, BY REGION    224

13.1         INTRODUCTION              225

13.2         NORTH AMERICA             225

13.2.1      NORTH AMERICA: MACROECONOMIC ANALYSIS                 226

13.2.2      US           231

13.2.2.1  US to dominate North American market during forecast period                 231

13.2.3      CANADA               236

13.2.3.1  Government support for expanding manufacturing facilities to propel market growth           236

13.3         EUROPE               239

13.3.1      EUROPE: MACROECONOMIC ANALYSIS 239

13.3.2      GERMANY           245

13.3.2.1  Growing pharmaceutical R&D and manufacturing to drive market    245

13.3.3      UK          249

13.3.3.1  Strong government support to propel market growth    249

13.3.4      FRANCE                253

13.3.4.1  Government investment in pharmaceutical industry to drive growth    253

13.3.5      ITALY    257

13.3.5.1  Initiatives for gene therapy development to drive growth                 257

13.3.6      SPAIN    260

13.3.6.1  Expansion of biomanufacturing facilities to support market growth    260

13.3.7      SWITZERLAND 264

13.3.7.1  Presence of key pharmaceutical and biopharmaceutical companies to support market growth                264

13.3.8      NETHERLANDS 268

13.3.8.1  Growing awareness and strong focus on pharmaceutical R&D to support market growth        268

13.3.9      REST OF EUROPE             271

13.4         ASIA PACIFIC     275

13.4.1      ASIA PACIFIC: MACROECONOMIC ANALYSIS       275

13.4.2      CHINA  280

13.4.2.1  China to dominate Asia Pacific market during forecast period                 280

13.4.3      JAPAN   284

13.4.3.1  Increasing initiatives supporting gene therapy adoption to propel market growth       284

13.4.4      INDIA    288

13.4.4.1  Favorable scenario for foreign direct investment to favor market growth    288

13.4.5      AUSTRALIA         292

13.4.5.1  Increasing demand for innovative therapies to propel market                 292

13.4.6      SOUTH KOREA  296

13.4.6.1  Increased export of drugs to support market growth      296

13.4.7      THAILAND          299

13.4.7.1  Favorable government policies to propel adoption of advanced therapies                 299

13.4.8      REST OF ASIA PACIFIC   303

13.5         LATIN AMERICA                307

13.5.1      LATIN AMERICA: MACROECONOMIC ANALYSIS 307

13.5.2      BRAZIL 312

13.5.2.1  Brazil to dominate LATAM market during forecast period                 312

13.5.3      MEXICO                315

13.5.3.1  Rising demand for chronic disease treatment to support market growth    315

13.5.4      REST OF LATIN AMERICA             319

13.6         MIDDLE EAST   323

13.6.1      MIDDLE EAST: MACROECONOMIC ANALYSIS     323

13.6.2      GCC COUNTRIES              328

13.6.2.1  Saudi Arabia          332

13.6.2.1.1                Growing healthcare expenditure to boost market growth                 332

13.6.2.2  UAE        336

13.6.2.2.1                Growing focus on genetic medicine development projects to drive market       336

13.6.2.3  Rest of GCC Countries        339

13.6.3      REST OF MIDDLE EAST 343

13.7         AFRICA 347

13.7.1      HIGH GROWTH POTENTIAL OF AFRICAN MARKETS TO ATTRACT KEY PLAYERS                347

13.7.2      AFRICA: MACROECONOMIC ANALYSIS  347

14            COMPETITIVE LANDSCAPE         352

14.1         OVERVIEW          352

14.2         KEY PLAYER STRATEGIES/RIGHT TO WIN, 2022–2024                 352

14.2.1      OVERVIEW OF STRATEGIES ADOPTED BY KEY PLAYERS IN GENE THERAPY MARKET, 2022−2024                 352

14.3         REVENUE ANALYSIS, 2021–2023  353

14.4         MARKET SHARE ANALYSIS, 2023                 354

14.5         COMPANY EVALUATION MATRIX: KEY PLAYERS, 2023                 356

14.5.1      STARS   357

14.5.2      EMERGING LEADERS     357

14.5.3      PERVASIVE PLAYERS      357

14.5.4      PARTICIPANTS 357

14.5.5      COMPETITIVE BENCHMARKING: KEY PLAYERS, 2023                 359

14.5.5.1  Company footprint               359

14.5.5.2  Region footprint   360

14.5.5.3  Therapy type footprint        361

14.5.5.4  Therapeutic area footprint  362

14.5.5.5  Route of administration footprint      363

14.6         COMPANY EVALUATION MATRIX: STARTUPS/SMES, 2023        364

14.6.1      PROGRESSIVE COMPANIES         364

14.6.2      RESPONSIVE COMPANIES            364

14.6.3      DYNAMIC COMPANIES  364

14.6.4      STARTING BLOCKS         364

14.6.5      COMPETITIVE BENCHMARKING: STARTUPS/SMES, 2023                 366

14.6.5.1  Detailed list of key startups/SMEs    366

14.6.5.2  Competitive benchmarking of key startups/SMEs          367

14.7         VALUATION & FINANCIAL METRICS       368

14.7.1      FINANCIAL METRICS      368

14.7.2      COMPANY VALUATION 368

14.8         BRAND/PRODUCT COMPARISON             369

14.9         COMPETITIVE SCENARIO             370

14.9.1      PRODUCT APPROVALS 370

14.9.2      DEALS  371

14.9.3      EXPANSIONS     373

15            COMPANY PROFILES      374

15.1         INTRODUCTION              374

15.2         KEY PLAYERS     374

15.2.1      BIOGEN INC.      374

15.2.1.1  Business overview 374

15.2.1.2  Products offered   375

15.2.1.3  Recent developments           376

15.2.1.3.1                Deals      376

15.2.1.4  MnM view              376

15.2.1.4.1                Key strengths        376

15.2.1.4.2                Strategic choices   377

15.2.1.4.3                Weaknesses and competitive threats 377

15.2.2      NOVARTIS AG   378

15.2.2.1  Business overview 378

15.2.2.2  Products offered   379

15.2.2.3  Recent developments           380

15.2.2.3.1                Deals      380

15.2.2.3.2                Expansions             380

15.2.2.3.3                Other developments             381

15.2.2.4  MnM view              381

15.2.2.4.1                Key strengths        381

15.2.2.4.2                Strategic choices   381

15.2.2.4.3                Weaknesses and competitive threats 381

15.2.3      ALNYLAM PHARMACEUTICALS, INC.      382

15.2.3.1  Business overview 382

15.2.3.2  Products offered   383

15.2.3.3  Recent developments           384

15.2.3.3.1                Product approvals 384

15.2.3.3.2                Deals      384

15.2.3.3.3                Other developments             385

15.2.3.4  MnM view              385

15.2.3.4.1                Key strengths        385

15.2.3.4.2                Strategic choices   385

15.2.3.4.3                Weaknesses and competitive threats 385

15.2.4      SAREPTA THERAPEUTICS, INC. 386

15.2.4.1  Business overview 386

15.2.4.2  Products offered   387

15.2.4.3  Recent developments           388

15.2.4.3.1                Product approvals 388

15.2.4.3.2                Deals      388

15.2.4.4  MnM view              389

15.2.4.4.1                Key strengths        389

15.2.4.4.2                Strategic choices   389

15.2.4.4.3                Weaknesses and competitive threats 389

15.2.5      JAZZ PHARMACEUTICALS PLC   390

15.2.5.1  Business overview 390

15.2.5.2  Products offered   391

15.2.5.3  Recent developments           392

15.2.5.3.1                Expansions             392

15.2.5.4  MnM view              392

15.2.5.4.1                Key strengths        392

15.2.5.4.2                Strategic choices   392

15.2.5.4.3                Weaknesses and competitive threats 392

15.2.6      FERRING B.V.     393

15.2.6.1  Business overview 393

15.2.6.2  Products offered   394

15.2.6.3  Recent developments           394

15.2.6.3.1                Product approvals 394

15.2.6.3.2                Deals      394

15.2.6.3.3                Expansions             395

15.2.7      PFIZER INC.        396

15.2.7.1  Business overview 396

15.2.7.2  Products offered   397

15.2.7.3  Recent developments           398

15.2.7.3.1                Product approvals 398

15.2.7.3.2                Deals      398

15.2.8      AMGEN, INC.      399

15.2.8.1  Business overview 399

15.2.8.2  Products offered   400

15.2.8.3  Recent developments           400

15.2.8.3.1                Deals      400

15.2.8.3.2                Expansions             400

15.2.9      JOHNSON & JOHNSON SERVICES, INC.   401

15.2.9.1  Business overview 401

15.2.9.2  Products offered   402

15.2.9.3  Recent developments           402

15.2.9.3.1                Deals      402

15.2.9.3.2                Other developments             403

15.2.10   DAIICHI SANKYO COMPANY, LIMITED. 404

15.2.10.1                 Business overview 404

15.2.10.2                 Products offered   405

15.2.11   BIOMARIN PHARMACEUTICAL INC.        406

15.2.11.1                 Business overview 406

15.2.11.2                 Products offered   407

15.2.11.3                 Recent developments           407

15.2.11.3.1             Product approvals 407

15.2.11.3.2             Expansions             408

15.2.12   KYOWA KIRIN CO., LTD.                409

15.2.12.1                 Business overview 409

15.2.12.2                 Products offered   410

15.2.12.3                 Recent developments           411

15.2.12.3.1             Product approvals 411

15.2.12.3.2             Deals      411

15.2.13   NIPPON SHINYAKU CO., LTD.    412

15.2.13.1                 Business overview 412

15.2.13.2                 Products offered   413

15.2.13.3                 Recent developments           414

15.2.13.3.1             Deals      414

15.2.14   PTC THERAPEUTICS      415

15.2.14.1                 Business overview 415

15.2.14.2                 Products offered   416

15.2.14.3                 Recent developments           416

15.2.14.3.1             Product approvals 416

15.2.15   UNIQURE NV.    417

15.2.15.1                 Business overview 417

15.2.15.2                 Products offered   418

15.2.15.3                 Recent developments           418

15.2.15.3.1             Deals      418

15.3         OTHER PLAYERS              419

15.3.1      JUVENTAS CELL THERAPY LTD.                419

15.3.2      CRISPR THERAPEUTICS                 419

15.3.3      BLUEBIRD BIO, INC.       420

15.3.4      KRYSTAL BIOTECH, INC.               421

15.3.5      SHANGHAI SUNWAY BIOTECH CO., LTD.              421

15.3.6      JW (CAYMAN) THERAPEUTICS CO. LTD 422

15.3.7      IASO BIOTECHNOLOGY                422

15.3.8      CARSGEN THERAPEUTICS HOLDINGS LIMITED 423

15.3.9      ADAPTIMMUNE                423

15.3.10   SIBIONO GENETECH CO. LTD.   424

15.3.11   ULTRAGENYX PHARMACEUTICAL INC. 424

16            APPENDIX           425

16.1         DISCUSSION GUIDE        425

16.2         KNOWLEDGESTORE: MARKETSANDMARKETS’ SUBSCRIPTION PORTAL                430

16.3         CUSTOMIZATION OPTIONS        432

16.4         RELATED REPORTS         432

16.5         AUTHOR DETAILS           433

LIST OF TABLES

TABLE 1                GENE THERAPY MARKET: INCLUSIONS & EXCLUSIONS      43

TABLE 2                IMPACT ANALYSIS OF SUPPLY-SIDE AND DEMAND-SIDE FACTORS              55

TABLE 3                GENE THERAPY MARKET: IMPACT ANALYSIS OF MARKET DYNAMICS       68

TABLE 4                GENE THERAPY MARKET: KEY PRODUCT APPROVALS, 2022–2024  69

TABLE 5                GENE THERAPY MARKET: INVESTMENTS AND FINANCING BY STARTUPS, 2024 70

TABLE 6                GENE THERAPY MARKET: LIST OF ADVANCED PLATFORMS LAUNCHED IN

2022–2024              71

TABLE 7                NUMBER OF CLINICAL TRIALS FOR GENE THERAPY DRUGS, 2024  72

TABLE 8                COST OF KEY GENE THERAPY PRODUCTS, 2024                 73

TABLE 9                GENE THERAPY MARKET: RAW MATERIAL VENDORS            83

TABLE 10              GENE THERAPY MARKET: PRODUCT VENDORS                 83

TABLE 11              GENE THERAPY MARKET: ROLE OF END USERS                 84

TABLE 12              GENE THERAPY MARKET: REGULATORY BODIES 84

TABLE 13              GENE THERAPY MARKET: INDICATIVE LIST OF PATENTS, 2023–2024        87

TABLE 14              GENE THERAPY PRODUCTS IN CLINICAL PIPELINE             88

TABLE 15              NORTH AMERICA: REGULATORY BODIES, GOVERNMENT AGENCIES, AND OTHER ORGANIZATIONS                 89

TABLE 16              EUROPE: REGULATORY BODIES, GOVERNMENT AGENCIES, AND OTHER ORGANIZATIONS           90

TABLE 17              ASIA PACIFIC: REGULATORY BODIES, GOVERNMENT AGENCIES, AND OTHER ORGANIZATIONS                 90

TABLE 18              REST OF THE WORLD: REGULATORY BODIES, GOVERNMENT AGENCIES, AND OTHER ORGANIZATIONS                 91

TABLE 19              COUNTRY-WISE REGULATORY SCENARIO FOR GENE THERAPY PRODUCTS        91

TABLE 20              US: REIMBURSEMENT CODES FOR GENE THERAPY PRODUCTS    93

TABLE 21              EUROPE: REIMBURSEMENT SCENARIO FOR GENE THERAPY PRODUCTS,

BY COUNTRY     94

TABLE 22              AVERAGE SELLING PRICE TREND OF GENE THERAPIES, BY KEY PLAYER,

2022–2024 (USD)                95

TABLE 23              AVERAGE SELLING PRICE TREND OF GENE THERAPIES, BY REGION,

2022–2024 (USD)                97

TABLE 24              GENE THERAPY MARKET: KEY CONFERENCES & EVENTS, 2025–2026           99

TABLE 25              GENE THERAPY MARKET: IMPACT OF PORTER’S FIVE FORCES      100

TABLE 26              INFLUENCE OF STAKEHOLDERS ON BUYING PROCESS (%)     103

TABLE 27              KEY BUYING CRITERIA FOR GENE THERAPY PRODUCTS, BY END USER            104

TABLE 28              GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)            109

TABLE 29              GENE SILENCING THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          110

TABLE 30              NORTH AMERICA: GENE SILENCING THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            110

TABLE 31              EUROPE: GENE SILENCING THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            111

TABLE 32              ASIA PACIFIC: GENE SILENCING THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            111

TABLE 33              LATIN AMERICA: GENE SILENCING THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            112

TABLE 34              MIDDLE EAST: GENE SILENCING THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            112

TABLE 35              GCC COUNTRIES: GENE SILENCING THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            112

TABLE 36              CELL REPLACEMENT THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          113

TABLE 37              NORTH AMERICA: CELL REPLACEMENT THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            114

TABLE 38              EUROPE: CELL REPLACEMENT THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            114

TABLE 39              ASIA PACIFIC: CELL REPLACEMENT THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            115

TABLE 40              LATIN AMERICA: CELL REPLACEMENT THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            115

TABLE 41              MIDDLE EAST: CELL REPLACEMENT THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            115

TABLE 42              GCC COUNTRIES: CELL REPLACEMENT THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            116

TABLE 43              GENE AUGMENTATION THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          117

TABLE 44              NORTH AMERICA: GENE AUGMENTATION THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            117

TABLE 45              EUROPE: GENE AUGMENTATION THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            118

TABLE 46              ASIA PACIFIC: GENE AUGMENTATION THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            118

TABLE 47              LATIN AMERICA: GENE AUGMENTATION THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            119

TABLE 48              MIDDLE EAST: GENE AUGMENTATION THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            119

TABLE 49              GCC COUNTRIES: GENE AUGMENTATION THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            119

TABLE 50              OTHER GENE THERAPIES MARKET, BY REGION, 2022–2032 (USD MILLION)            120

TABLE 51              NORTH AMERICA: OTHER GENE THERAPIES MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            121

TABLE 52              EUROPE: OTHER GENE THERAPIES MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            121

TABLE 53              ASIA PACIFIC: OTHER GENE THERAPIES MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            122

TABLE 54              LATIN AMERICA: OTHER GENE THERAPIES MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            122

TABLE 55              MIDDLE EAST: OTHER GENE THERAPIES MARKET, BY REGION,

2022–2032 (USD MILLION)            122

TABLE 56              GCC COUNTRIES: OTHER GENE THERAPIES MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            123

TABLE 57              GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)       125

TABLE 58              VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            126

TABLE 59              VIRAL VECTOR-BASED GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            126

TABLE 60              NORTH AMERICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 126

TABLE 61              EUROPE: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            127

TABLE 62              ASIA PACIFIC: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 127

TABLE 63              LATIN AMERICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 128

TABLE 64              MIDDLE EAST: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            128

TABLE 65              GCC COUNTRIES: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 128

TABLE 66              RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)       129

TABLE 67              RETROVIRAL VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)            129

TABLE 68              NORTH AMERICA: RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            130

TABLE 69              EUROPE: RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            130

TABLE 70              ASIA PACIFIC: RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            131

TABLE 71              LATIN AMERICA: RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            131

TABLE 72             MIDDLE EAST: RETROVIRAL VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            131

TABLE 73              GCC COUNTRIES: RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)          132

TABLE 74              GAMMA RETROVIRAL VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)          132

TABLE 75              NORTH AMERICA: GAMMA RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            133

TABLE 76              EUROPE: GAMMA RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            133

TABLE 77              ASIA PACIFIC: GAMMA RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            134

TABLE 78              LATIN AMERICA: GAMMA RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            134

TABLE 79              MIDDLE EAST: GAMMA RETROVIRAL VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            134

TABLE 80              GCC COUNTRIES: GAMMA RETROVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            135

TABLE 81              LENTIVIRAL VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)            136

TABLE 82              NORTH AMERICA: LENTIVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            136

TABLE 83              EUROPE: LENTIVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            136

TABLE 84              ASIA PACIFIC: LENTIVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            137

TABLE 85              LATIN AMERICA: LENTIVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            137

TABLE 86              MIDDLE EAST: LENTIVIRAL VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            137

TABLE 87              GCC COUNTRIES: LENTIVIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            138

TABLE 88              AAV VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION) 138

TABLE 89              NORTH AMERICA: AAV VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            139

TABLE 90              EUROPE: AAV VECTORS MARKET, BY COUNTRY, 2022–2032 (USD MILLION)            139

TABLE 91              ASIA PACIFIC: AAV VECTORS MARKET, BY COUNTRY, 2022–2032 (USD MILLION)     140

TABLE 92              LATIN AMERICA: AAV VECTORS MARKET, BY COUNTRY, 2022–2032 (USD MILLION)     140

TABLE 93              MIDDLE EAST: AAV VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)          140

TABLE 94              GCC COUNTRIES: AAV VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            141

TABLE 95              OTHER VIRAL VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)            141

TABLE 96              NORTH AMERICA: OTHER VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            142

TABLE 97              EUROPE: OTHER VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            142

TABLE 98              ASIA PACIFIC: OTHER VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            143

TABLE 99              LATIN AMERICA: OTHER VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            143

TABLE 100            MIDDLE EAST: OTHER VIRAL VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            143

TABLE 101            GCC COUNTRIES: OTHER VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            144

TABLE 102            NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            144

TABLE 103            NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            145

TABLE 104            NORTH AMERICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               145

TABLE 105            EUROPE: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 146

TABLE 106            ASIA PACIFIC: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)            146

TABLE 107            LATIN AMERICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               147

TABLE 108            MIDDLE EAST: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)                 147

TABLE 109            GCC COUNTRIES: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               147

TABLE 110            OLIGONUCLEOTIDE VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)          148

TABLE 111            NORTH AMERICA: OLIGONUCLEOTIDE VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            148

TABLE 112            EUROPE: OLIGONUCLEOTIDE VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            149

TABLE 113            ASIA PACIFIC: OLIGONUCLEOTIDE VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            149

TABLE 114            LATIN AMERICA: OLIGONUCLEOTIDE VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            150

TABLE 115            MIDDLE EAST: OLIGONUCLEOTIDE VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            150

TABLE 116            GCC COUNTRIES: OLIGONUCLEOTIDE VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            150

TABLE 117            OTHER NON-VIRAL VECTORS MARKET, BY REGION, 2022–2032 (USD MILLION)          151

TABLE 118            NORTH AMERICA: OTHER NON-VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)          151

TABLE 119            EUROPE: OTHER NON-VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            152

TABLE 120            ASIA PACIFIC: OTHER NON-VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            152

TABLE 121            LATIN AMERICA: OTHER NON-VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            153

TABLE 122            MIDDLE EAST: OTHER NON-VIRAL VECTORS MARKET, BY REGION,

2022–2032 (USD MILLION)            153

TABLE 123            GCC COUNTRIES: OTHER NON-VIRAL VECTORS MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            153

TABLE 124            GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)       155

TABLE 125            DEFICIENCY GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          156

TABLE 126            NORTH AMERICA: DEFICIENCY GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            156

TABLE 127            EUROPE: DEFICIENCY GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)          157

TABLE 128            ASIA PACIFIC: DEFICIENCY GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            157

TABLE 129            LATIN AMERICA: GENE THERAPY MARKET FOR DEFICIENCY GENES, BY COUNTRY, 2022–2032 (USD MILLION)                 158

TABLE 130            MIDDLE EAST: GENE THERAPY MARKET FOR DEFICIENCY GENES, BY REGION, 2022–2032 (USD MILLION)                 158

TABLE 131            GCC COUNTRIES: GENE THERAPY MARKET FOR DEFICIENCY GENES, BY COUNTRY, 2022–2032 (USD MILLION)                 158

TABLE 132            RECEPTOR GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          159

TABLE 133            NORTH AMERICA: RECEPTOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            159

TABLE 134            EUROPE: RECEPTOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            160

TABLE 135            ASIA PACIFIC: RECEPTOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            160

TABLE 136            LATIN AMERICA: RECEPTOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            161

TABLE 137            MIDDLE EAST: RECEPTOR GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            161

TABLE 138            GCC COUNTRIES: RECEPTOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            161

TABLE 139            ANTIGEN GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)            162

TABLE 140            NORTH AMERICA: ANTIGEN GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            163

TABLE 141            EUROPE: ANTIGEN GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            163

TABLE 142            ASIA PACIFIC: ANTIGEN GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            164

TABLE 143            LATIN AMERICA: ANTIGEN GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            164

TABLE 144            MIDDLE EAST: ANTIGEN GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            164

TABLE 145            GCC COUNTRIES: ANTIGEN GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            165

TABLE 146            CYTOKINE GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          166

TABLE 147            NORTH AMERICA: CYTOKINE GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            166

TABLE 148            EUROPE: CYTOKINE GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            167

TABLE 149            ASIA PACIFIC: CYTOKINE GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            167

TABLE 150            LATIN AMERICA: CYTOKINE GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            168

TABLE 151            MIDDLE EAST: CYTOKINE GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            168

TABLE 152            GCC COUNTRIES: CYTOKINE GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            168

TABLE 153            TUMOR SUPPRESSOR GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            169

TABLE 154            NORTH AMERICA: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 170

TABLE 155            EUROPE: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            170

TABLE 156            ASIA PACIFIC: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 171

TABLE 157            LATIN AMERICA: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 171

TABLE 158            MIDDLE EAST: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            171

TABLE 159            GCC COUNTRIES: TUMOR SUPPRESSOR GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)                 172

TABLE 160            GENE THERAPY MARKET FOR OTHER GENES, BY REGION,

2022–2032 (USD MILLION)            173

TABLE 161            NORTH AMERICA: GENE THERAPY MARKET FOR OTHER GENES, BY COUNTRY, 2022–2032 (USD MILLION)                 173

TABLE 162            EUROPE: GENE THERAPY MARKET FOR OTHER GENES, BY COUNTRY,

2022–2032 (USD MILLION)            174

TABLE 163            ASIA PACIFIC: GENE THERAPY MARKET FOR OTHER GENES, BY COUNTRY,

2022–2032 (USD MILLION)            174

TABLE 164            LATIN AMERICA: GENE THERAPY MARKET FOR OTHER GENES, BY COUNTRY, 2022–2032 (USD MILLION)                 175

TABLE 165            MIDDLE EAST: GENE THERAPY MARKET FOR OTHER GENES, BY REGION,

2022–2032 (USD MILLION)            175

TABLE 166            GCC COUNTRIES: GENE THERAPY MARKET FOR OTHER GENES, BY COUNTRY, 2022–2032 (USD MILLION)                 175

TABLE 167            GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2022–2032 (USD MILLION)               177

TABLE 168            GENE THERAPY MARKET FOR NEUROLOGY, BY REGION,

2022–2032 (USD MILLION)            178

TABLE 169            NORTH AMERICA: GENE THERAPY MARKET FOR NEUROLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            178

TABLE 170            EUROPE: GENE THERAPY MARKET FOR NEUROLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            179

TABLE 171            ASIA PACIFIC: GENE THERAPY MARKET FOR NEUROLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            179

TABLE 172            LATIN AMERICA: GENE THERAPY MARKET FOR NEUROLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            180

TABLE 173            MIDDLE EAST: GENE THERAPY MARKET FOR NEUROLOGY, BY REGION,

2022–2032 (USD MILLION)            180

TABLE 174            GCC COUNTRIES: GENE THERAPY MARKET FOR NEUROLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            180

TABLE 175            GENE THERAPY MARKET FOR ONCOLOGY, BY REGION, 2022–2032 (USD MILLION)          181

TABLE 176            NORTH AMERICA: GENE THERAPY MARKET FOR ONCOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            182

TABLE 177            EUROPE: GENE THERAPY MARKET FOR ONCOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)          182

TABLE 178            ASIA PACIFIC: GENE THERAPY MARKET FOR ONCOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            183

TABLE 179            LATIN AMERICA: GENE THERAPY MARKET FOR ONCOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            183

TABLE 180            MIDDLE EAST: GENE THERAPY MARKET FOR ONCOLOGY, BY REGION,

2022–2032 (USD MILLION)            183

TABLE 181            GCC COUNTRIES: GENE THERAPY MARKET FOR ONCOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            184

TABLE 182            GENE THERAPY MARKET FOR HEMATOLOGY, BY REGION,

2022–2032 (USD MILLION)            185

TABLE 183            NORTH AMERICA: GENE THERAPY MARKET FOR HEMATOLOGY, BY COUNTRY, 2022–2032 (USD MILLION)                 185

TABLE 184            EUROPE: GENE THERAPY MARKET FOR HEMATOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            186

TABLE 185            ASIA PACIFIC: GENE THERAPY MARKET FOR HEMATOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            186

TABLE 186            LATIN AMERICA: GENE THERAPY MARKET FOR HEMATOLOGY, BY COUNTRY,

2022–2032 (USD MILLION)            187

TABLE 187            MIDDLE EAST: GENE THERAPY MARKET FOR HEMATOLOGY, BY REGION,

2022–2032 (USD MILLION)            187

TABLE 188            GCC COUNTRIES: GENE THERAPY MARKET FOR HEMATOLOGY, BY COUNTRY, 2022–2032 (USD MILLION)                 187

TABLE 189            GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS, BY REGION,

2022–2032 (USD MILLION)            188

TABLE 190            NORTH AMERICA: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS,

BY COUNTRY, 2022–2032 (USD MILLION)               188

TABLE 191            EUROPE: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS, BY COUNTRY, 2022–2032 (USD MILLION)                 189

TABLE 192            ASIA PACIFIC: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS,

BY COUNTRY, 2022–2032 (USD MILLION)               189

TABLE 193            LATIN AMERICA: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS,

BY COUNTRY, 2022–2032 (USD MILLION)               190

TABLE 194            MIDDLE EAST: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS,

BY REGION, 2022–2032 (USD MILLION)   190

TABLE 195            GCC COUNTRIES: GENE THERAPY MARKET FOR OTHER THERAPEUTIC AREAS,

BY COUNTRY, 2022–2032 (USD MILLION)               190

TABLE 196            GENE THERAPY MARKET, BY DELIVERY METHOD, 2022–2032 (USD MILLION)       192

TABLE 197            IN VIVO GENE THERAPY: COMMERCIALIZED AND PIPELINE PRODUCTS           193

TABLE 198            IN VIVO GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)            193

TABLE 199            NORTH AMERICA: IN VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            194

TABLE 200            EUROPE: IN VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            194

TABLE 201            ASIA PACIFIC: IN VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            195

TABLE 202            LATIN AMERICA: IN VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            195

TABLE 203            MIDDLE EAST: IN VIVO GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            195

TABLE 204            GCC COUNTRIES: IN VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            196

TABLE 205            EX VIVO GENE THERAPY: COMMERCIALIZED AND PIPELINE PRODUCTS           197

TABLE 206            EX VIVO GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)            197

TABLE 207            NORTH AMERICA: EX VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            197

TABLE 208            EUROPE: EX VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            198

TABLE 209            APAC: EX VIVO GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)     198

TABLE 210            LATIN AMERICA: EX VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            199

TABLE 211            MIDDLE EAST: EX VIVO GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            199

TABLE 212            GCC COUNTRIES: EX VIVO GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            199

TABLE 213            GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            201

TABLE 214            EXAMPLES OF INTRAVENOUSLY DELIVERED GENE THERAPY                 201

TABLE 215            INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            202

TABLE 216            NORTH AMERICA: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               202

TABLE 217            EUROPE: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)            203

TABLE 218            ASIA PACIFIC: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               203

TABLE 219            LATIN AMERICA: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               204

TABLE 220            MIDDLE EAST: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET,

BY REGION, 2022–2032 (USD MILLION)   204

TABLE 221            GCC COUNTRIES: INTRAVENOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               204

TABLE 222            SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET, BY REGION,

2022–2032 (USD MILLION)            205

TABLE 223            NORTH AMERICA: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)             206

TABLE 224            EUROPE: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               206

TABLE 225            ASIA PACIFIC: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               207

TABLE 226            LATIN AMERICA: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               207

TABLE 227            MIDDLE EAST: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY REGION, 2022–2032 (USD MILLION)   207

TABLE 228            GCC COUNTRIES: SUBCUTANEOUSLY ADMINISTERED GENE THERAPY MARKET,

BY COUNTRY, 2022–2032 (USD MILLION)               208

TABLE 229            EXAMPLE OF GENE THERAPIES ADMINISTERED THROUGH OTHER ROUTES        208

TABLE 230            GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY REGION, 2022–2032 (USD MILLION)                 209

TABLE 231            NORTH AMERICA: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY COUNTRY, 2022–2032 (USD MILLION)       209

TABLE 232            EUROPE: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION,

BY COUNTRY, 2022–2032 (USD MILLION)               210

TABLE 233            ASIA PACIFIC: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY COUNTRY, 2022–2032 (USD MILLION) 210

TABLE 234            LATIN AMERICA: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY COUNTRY, 2022–2032 (USD MILLION) 211

TABLE 235            MIDDLE EAST: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY REGION, 2022–2032 (USD MILLION) 211

TABLE 236            GCC COUNTRIES: GENE THERAPY MARKET FOR OTHER ROUTES OF ADMINISTRATION, BY COUNTRY, 2022–2032 (USD MILLION) 211

TABLE 237            GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)       213

TABLE 238            GENE THERAPY MARKET FOR HOSPITALS, BY REGION, 2022–2032 (USD MILLION)          214

TABLE 239            NORTH AMERICA: GENE THERAPY MARKET FOR HOSPITALS, BY COUNTRY,

2022–2032 (USD MILLION)            214

TABLE 240            EUROPE: GENE THERAPY MARKET FOR HOSPITALS, BY COUNTRY,

2022–2032 (USD MILLION)            215

TABLE 241            ASIA PACIFIC: GENE THERAPY MARKET FOR HOSPITALS, BY COUNTRY,

2022–2032 (USD MILLION)            215

TABLE 242            LATIN AMERICA: GENE THERAPY MARKET FOR HOSPITALS, BY COUNTRY,

2022–2032 (USD MILLION)            216

TABLE 243            MIDDLE EAST: GENE THERAPY MARKET FOR HOSPITALS, BY REGION,

2022–2032 (USD MILLION)            216

TABLE 244            GCC COUNTRIES: GENE THERAPY MARKET FOR HOSPITALS, BY COUNTRY,

2022–2032 (USD MILLION)            216

TABLE 245            GENE THERAPY MARKET FOR SPECIALTY CENTERS, BY REGION,

2022–2032 (USD MILLION)            217

TABLE 246            NORTH AMERICA: GENE THERAPY MARKET FOR SPECIALTY CENTERS,

BY COUNTRY, 2022–2032 (USD MILLION)               218

TABLE 247            EUROPE: GENE THERAPY MARKET FOR SPECIALTY CENTERS, BY COUNTRY,

2022–2032 (USD MILLION)            218

TABLE 248            ASIA PACIFIC: GENE THERAPY MARKET FOR SPECIALTY CENTERS, BY COUNTRY, 2022–2032 (USD MILLION)                 219

TABLE 249            LATIN AMERICA: GENE THERAPY MARKET FOR SPECIALTY CENTERS, BY COUNTRY, 2022–2032 (USD MILLION)                 219

TABLE 250            MIDDLE EAST: GENE THERAPY MARKET FOR SPECIALTY CENTERS, BY REGION, 2022–2032 (USD MILLION)                 219

TABLE 251            GCC COUNTRIES: GENE THERAPY MARKET FOR SPECIALTY CENTERS,

BY COUNTRY, 2022–2032 (USD MILLION)               220

TABLE 252            GENE THERAPY MARKET FOR OTHER END USERS, BY REGION,

2022–2032 (USD MILLION)            221

TABLE 253            NORTH AMERICA: GENE THERAPY MARKET FOR OTHER END USERS, BY COUNTRY, 2022–2032 (USD MILLION)            221

TABLE 254            EUROPE: GENE THERAPY MARKET FOR OTHER END USERS, BY COUNTRY,

2022–2032 (USD MILLION)            222

TABLE 255            ASIA PACIFIC GENE THERAPY MARKET FOR OTHER END USERS, BY COUNTRY, 2022–2032 (USD MILLION)                 222

TABLE 256            LATIN AMERICA: GENE THERAPY MARKET FOR OTHER END USERS, BY COUNTRY, 2022–2032 (USD MILLION)                 223

TABLE 257            MIDDLE EAST: GENE THERAPY MARKET FOR OTHER END USERS, BY REGION, 2022–2032 (USD MILLION)                 223

TABLE 258            GCC COUNTRIES: GENE THERAPY MARKET FOR OTHER END USERS, BY COUNTRY, 2022–2032 (USD MILLION)                 223

TABLE 259            GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION) 225

TABLE 260            NORTH AMERICA: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET             226

TABLE 261            NORTH AMERICA: GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            227

TABLE 262            NORTH AMERICA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            228

TABLE 263            NORTH AMERICA: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            228

TABLE 264            NORTH AMERICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            228

TABLE 265            NORTH AMERICA: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            229

TABLE 266            NORTH AMERICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 229

TABLE 267            NORTH AMERICA: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            229

TABLE 268            NORTH AMERICA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            230

TABLE 269            NORTH AMERICA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            230

TABLE 270            NORTH AMERICA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)                 230

TABLE 271            NORTH AMERICA: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)          231

TABLE 272            US FDA APPROVALS FOR GENE THERAPY PRODUCTS, 2022–2024    232

TABLE 273          US: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)            232

TABLE 274            US: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)       233

TABLE 275            US: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            233

TABLE 276            US: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)            233

TABLE 277            US: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            234

TABLE 278            US: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            234

TABLE 279            US: GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2022–2032 (USD MILLION)               234

TABLE 280            US: GENE THERAPY MARKET, BY DELIVERY METHOD, 2022–2032 (USD MILLION)       235

TABLE 281            US: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            235

TABLE 282            US: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            235

TABLE 283            CANADA: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)           236

TABLE 284            CANADA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            236

TABLE 285            CANADA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            237

TABLE 286            CANADA: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                237

TABLE 287            CANADA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            237

TABLE 288            CANADA: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                238

TABLE 289            CANADA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            238

TABLE 290            CANADA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            238

TABLE 291            CANADA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            239

TABLE 292            CANADA: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                239

TABLE 293            EUROPE: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET              240

TABLE 294            EUROPE: GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)     242

TABLE 295            EUROPE: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)           242

TABLE 296            EUROPE: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            242

TABLE 297            EUROPE: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            243

TABLE 298            EUROPE: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                243

TABLE 299            EUROPE: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            243

TABLE 300            EUROPE: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                244

TABLE 301            EUROPE: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            244

TABLE 302            EUROPE: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            244

TABLE 303            EUROPE: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            245

TABLE 304            EUROPE: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                245

TABLE 305            GERMANY: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)          246

TABLE 306            GERMANY: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         246

TABLE 307            GERMANY: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)          246

TABLE 308            GERMANY: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                247

TABLE 309            GERMANY: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            247

TABLE 310            GERMANY: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                247

TABLE 311            GERMANY: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            248

TABLE 312            GERMANY: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            248

TABLE 313            GERMANY: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            248

TABLE 314            GERMANY: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                249

TABLE 315            UK: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                249

TABLE 316            UK: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)       250

TABLE 317            UK: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            250

TABLE 318            UK: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)            250

TABLE 319            UK: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            251

TABLE 320            UK: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            251

TABLE 321            UK: GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2022–2032 (USD MILLION)               251

TABLE 322            UK: GENE THERAPY MARKET, BY DELIVERY METHOD, 2022–2032 (USD MILLION)       252

TABLE 323            UK: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            252

TABLE 324            UK: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            252

TABLE 325            FRANCE: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                253

TABLE 326            FRANCE: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            254

TABLE 327            FRANCE: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            254

TABLE 328            FRANCE: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                254

TABLE 329            FRANCE: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            255

TABLE 330            FRANCE: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                255

TABLE 331            FRANCE: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            255

TABLE 332            FRANCE: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            256

TABLE 333            FRANCE: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            256

TABLE 334            FRANCE: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                256

TABLE 335            ITALY: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                257

TABLE 336            ITALY: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            257

TABLE 337            ITALY: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            258

TABLE 338            ITALY: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                258

TABLE 339            ITALY: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            258

TABLE 340            ITALY: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            259

TABLE 341            ITALY: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            259

TABLE 342            ITALY: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            259

TABLE 343            ITALY: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            260

TABLE 344            ITALY: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            260

TABLE 345            SPAIN: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                261

TABLE 346            SPAIN: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            261

TABLE 347            SPAIN: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            261

TABLE 348            SPAIN: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                262

TABLE 349            SPAIN: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            262

TABLE 350            SPAIN: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            262

TABLE 351            SPAIN: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            263

TABLE 352            SPAIN: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            263

TABLE 353            SPAIN: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            263

TABLE 354            SPAIN: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            264

TABLE 355            SWITZERLAND: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            264

TABLE 356            SWITZERLAND: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         265

TABLE 357            SWITZERLAND: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            265

TABLE 358            SWITZERLAND: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            265

TABLE 359            SWITZERLAND: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 266

TABLE 360            SWITZERLAND: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            266

TABLE 361            SWITZERLAND: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            266

TABLE 362            SWITZERLAND: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            267

TABLE 363            SWITZERLAND: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            267

TABLE 364            SWITZERLAND: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            267

TABLE 365            NETHERLANDS: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            268

TABLE 366            NETHERLANDS: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         268

TABLE 367            NETHERLANDS: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            269

TABLE 368            NETHERLANDS: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            269

TABLE 369            NETHERLANDS: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 269

TABLE 370            NETHERLANDS: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            270

TABLE 371            NETHERLANDS: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            270

TABLE 372            NETHERLANDS: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            270

TABLE 373            NETHERLANDS: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            271

TABLE 374            NETHERLANDS: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)          271

TABLE 375            REST OF EUROPE: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            272

TABLE 376            REST OF EUROPE: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            272

TABLE 377            REST OF EUROPE: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 272

TABLE 378            REST OF EUROPE: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            273

TABLE 379            REST OF EUROPE: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 273

TABLE 380            REST OF EUROPE: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            273

TABLE 381            REST OF EUROPE: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            274

TABLE 382            REST OF EUROPE: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            274

TABLE 383            REST OF EUROPE: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)                 274

TABLE 384            REST OF EUROPE: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            275

TABLE 385            ASIA PACIFIC: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET    276

TABLE 386            ASIA PACIFIC: GENE THERAPY MARKET, BY COUNTRY, 2022–2032 (USD MILLION)     277

TABLE 387            ASIA PACIFIC: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            277

TABLE 388            ASIA PACIFIC: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         277

TABLE 389            ASIA PACIFIC: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            278

TABLE 390            ASIA PACIFIC: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            278

TABLE 391            ASIA PACIFIC: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 278

TABLE 392            ASIA PACIFIC: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            279

TABLE 393            ASIA PACIFIC: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            279

TABLE 394            ASIA PACIFIC: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            279

TABLE 395            ASIA PACIFIC: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            280

TABLE 396            ASIA PACIFIC: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                280

TABLE 397            CHINA: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                281

TABLE 398            CHINA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            281

TABLE 399            CHINA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            281

TABLE 400            CHINA: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                282

TABLE 401            CHINA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            282

TABLE 402            CHINA: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                282

TABLE 403            CHINA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            283

TABLE 404            CHINA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            283

TABLE 405            CHINA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            283

TABLE 406            CHINA: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            284

TABLE 407            JAPAN: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                285

TABLE 408            JAPAN: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            285

TABLE 409            JAPAN: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            285

TABLE 410            JAPAN: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                286

TABLE 411            JAPAN: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            286

TABLE 412          JAPAN: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            286

TABLE 413            JAPAN: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            287

TABLE 414            JAPAN: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            287

TABLE 415            JAPAN: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            287

TABLE 416            JAPAN: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            288

TABLE 417            INDIA: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                289

TABLE 418            INDIA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            289

TABLE 419            INDIA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            289

TABLE 420            INDIA: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                290

TABLE 421            INDIA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            290

TABLE 422            INDIA: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            290

TABLE 423            INDIA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            291

TABLE 424            INDIA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            291

TABLE 425            INDIA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            291

TABLE 426            INDIA: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            292

TABLE 427            AUSTRALIA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            292

TABLE 428            AUSTRALIA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         293

TABLE 429            AUSTRALIA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            293

TABLE 430            AUSTRALIA: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)         293

TABLE 431            AUSTRALIA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            294

TABLE 432            AUSTRALIA: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                294

TABLE 433            AUSTRALIA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            294

TABLE 434            AUSTRALIA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            295

TABLE 435            AUSTRALIA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            295

TABLE 436            AUSTRALIA: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                295

TABLE 437            SOUTH KOREA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            296

TABLE 438            SOUTH KOREA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         296

TABLE 439            SOUTH KOREA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            297

TABLE 440            SOUTH KOREA: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            297

TABLE 441            SOUTH KOREA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 297

TABLE 442            SOUTH KOREA: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            298

TABLE 443            SOUTH KOREA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            298

TABLE 444            SOUTH KOREA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            298

TABLE 445            SOUTH KOREA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            299

TABLE 446            SOUTH KOREA: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            299

TABLE 447            THAILAND: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            300

TABLE 448            THAILAND: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         300

TABLE 449            THAILAND: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            300

TABLE 450            THAILAND: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)         301

TABLE 451            THAILAND: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)          301

TABLE 452            THAILAND: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                301

TABLE 453            THAILAND: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            302

TABLE 454            THAILAND: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            302

TABLE 455            THAILAND: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            302

TABLE 456            THAILAND: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                303

TABLE 457          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            303

TABLE 458          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            304

TABLE 459            REST OF ASIA PACIFIC: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 304

TABLE 460            REST OF ASIA PACIFIC: RETROVIRAL VECTORS MARKET, BY TYPE

2022–2032 (USD MILLION)            304

TABLE 461            REST OF ASIA PACIFIC: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY TYPE, 2022–2032 (USD MILLION)         305

TABLE 462          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            305

TABLE 463          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            305

TABLE 464          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            306

TABLE 465          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)                 306

TABLE 466          REST OF ASIA PACIFIC: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            306

TABLE 467            LATIN AMERICA: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET    308

TABLE 468            LATIN AMERICA: GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            308

TABLE 469            LATIN AMERICA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            308

TABLE 470            LATIN AMERICA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         309

TABLE 471            LATIN AMERICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            309

TABLE 472            LATIN AMERICA: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            309

TABLE 473            LATIN AMERICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 310

TABLE 474            LATIN AMERICA: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            310

TABLE 475            LATIN AMERICA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            310

TABLE 476            LATIN AMERICA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)          311

TABLE 477            LATIN AMERICA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            311

TABLE 478            LATIN AMERICA: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            311

TABLE 479            BRAZIL: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                312

TABLE 480            BRAZIL: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            312

TABLE 481            BRAZIL: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            313

TABLE 482            BRAZIL: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                313

TABLE 483            BRAZIL: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            313

TABLE 484            BRAZIL: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                314

TABLE 485            BRAZIL: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            314

TABLE 486            BRAZIL: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            314

TABLE 487            BRAZIL: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            315

TABLE 488          BRAZIL: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            315

TABLE 489            MEXICO: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                316

TABLE 490            MEXICO: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            316

TABLE 491            MEXICO: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            316

TABLE 492            MEXICO: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                317

TABLE 493            MEXICO: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            317

TABLE 494            MEXICO: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                317

TABLE 495            MEXICO: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            318

TABLE 496            MEXICO: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            318

TABLE 497            MEXICO: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            318

TABLE 498            MEXICO: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)                319

TABLE 499            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            319

TABLE 500            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            320

TABLE 501            REST OF LATIN AMERICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)            320

TABLE 502            REST OF LATIN AMERICA: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            320

TABLE 503            REST OF LATIN AMERICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY TYPE, 2022–2032 (USD MILLION)         321

TABLE 504            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            321

TABLE 505            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            321

TABLE 506            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            322

TABLE 507            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)            322

TABLE 508            REST OF LATIN AMERICA: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            322

TABLE 509            MIDDLE EAST: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET    324

TABLE 510            MIDDLE EAST: GENE THERAPY MARKET, BY REGION, 2022–2032 (USD MILLION)          324

TABLE 511            MIDDLE EAST: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            324

TABLE 512            MIDDLE EAST: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         325

TABLE 513            MIDDLE EAST: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            325

TABLE 514          MIDDLE EAST: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            325

TABLE 515            MIDDLE EAST: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 326

TABLE 516            MIDDLE EAST: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            326

TABLE 517            MIDDLE EAST: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            326

TABLE 518            MIDDLE EAST: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            327

TABLE 519            MIDDLE EAST: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            327

TABLE 520            MIDDLE EAST: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            327

TABLE 521            GCC COUNTRIES: GENE THERAPY MARKET, BY COUNTRY,

2022–2032 (USD MILLION)            328

TABLE 522            GCC COUNTRIES: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            328

TABLE 523            GCC COUNTRIES: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            329

TABLE 524            GCC COUNTRIES: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            329

TABLE 525            GCC COUNTRIES: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            329

TABLE 526            GCC COUNTRIES: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 330

TABLE 527            GCC COUNTRIES: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            330

TABLE 528            GCC COUNTRIES: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            330

TABLE 529            GCC COUNTRIES: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            331

TABLE 530            GCC COUNTRIES: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)                 331

TABLE 531            GCC COUNTRIES: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            331

TABLE 532            SAUDI ARABIA: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            332

TABLE 533            SAUDI ARABIA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)         333

TABLE 534            SAUDI ARABIA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            333

TABLE 535          SAUDI ARABIA: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            333

TABLE 536            SAUDI ARABIA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 334

TABLE 537            SAUDI ARABIA: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            334

TABLE 538            SAUDI ARABIA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            334

TABLE 539            SAUDI ARABIA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            335

TABLE 540            SAUDI ARABIA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            335

TABLE 541            SAUDI ARABIA: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            335

TABLE 542            UAE: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                336

TABLE 543            UAE: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            336

TABLE 544            UAE: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            337

TABLE 545            UAE: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)            337

TABLE 546            UAE: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            337

TABLE 547            UAE: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)            338

TABLE 548            UAE: GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2022–2032 (USD MILLION)                338

TABLE 549            UAE: GENE THERAPY MARKET, BY DELIVERY METHOD, 2022–2032 (USD MILLION)       338

TABLE 550            UAE: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            339

TABLE 551            UAE: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            339

TABLE 552            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)          340

TABLE 553            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            340

TABLE 554            REST OF GCC COUNTRIES: VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY TYPE, 2022–2032 (USD MILLION)         340

TABLE 555            REST OF GCC COUNTRIES: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            341

TABLE 556            REST OF GCC COUNTRIES: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY TYPE, 2022–2032 (USD MILLION)         341

TABLE 557            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            341

TABLE 558            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2022–2032 (USD MILLION)                 342

TABLE 559            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY DELIVERY METHOD, 2022–2032 (USD MILLION)                 342

TABLE 560            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)            342

TABLE 561            REST OF GCC COUNTRIES: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            343

TABLE 562            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY THERAPY TYPE,

2022–2032 (USD MILLION)            343

TABLE 563            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY VECTOR,

2022–2032 (USD MILLION)            344

TABLE 564            REST OF MIDDLE EAST: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE, 2022–2032 (USD MILLION)                 344

TABLE 565            REST OF MIDDLE EAST: RETROVIRAL VECTORS MARKET, BY TYPE,

2022–2032 (USD MILLION)            344

TABLE 566            REST OF MIDDLE EAST: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET,

BY TYPE, 2022–2032 (USD MILLION)         345

TABLE 567            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY GENE TYPE,

2022–2032 (USD MILLION)            345

TABLE 568            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            345

TABLE 569            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            346

TABLE 570            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2022–2032 (USD MILLION)            346

TABLE 571            REST OF MIDDLE EAST: GENE THERAPY MARKET, BY END USER,

2022–2032 (USD MILLION)            346

TABLE 572            AFRICA: MACROECONOMIC OUTLOOK FOR GENE THERAPY MARKET              348

TABLE 573            AFRICA: GENE THERAPY MARKET, BY THERAPY TYPE, 2022–2032 (USD MILLION)                348

TABLE 574            AFRICA: GENE THERAPY MARKET, BY VECTOR, 2022–2032 (USD MILLION)            349

TABLE 575            AFRICA: VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            349

TABLE 576            AFRICA: RETROVIRAL VECTORS MARKET, BY TYPE, 2022–2032 (USD MILLION)                349

TABLE 577            AFRICA: NON-VIRAL VECTOR-BASED GENE THERAPY MARKET, BY TYPE,

2022–2032 (USD MILLION)            350

TABLE 578            AFRICA: GENE THERAPY MARKET, BY GENE TYPE, 2022–2032 (USD MILLION)                350

TABLE 579            AFRICA: GENE THERAPY MARKET, BY THERAPEUTIC AREA,

2022–2032 (USD MILLION)            350

TABLE 580            AFRICA: GENE THERAPY MARKET, BY DELIVERY METHOD,

2022–2032 (USD MILLION)            351

TABLE 581            AFRICA: GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION,

2022–2032 (USD MILLION)            351

TABLE 582          AFRICA: GENE THERAPY MARKET, BY END USER, 2022–2032 (USD MILLION)            351

TABLE 583            STRATEGIES DEPLOYED BY KEY COMPANIES IN GENE THERAPY MARKET              352

TABLE 584            GENE THERAPY MARKET: DEGREE OF COMPETITION 355

TABLE 585            GENE THERAPY MARKET: REGION FOOTPRINT                 360

TABLE 586            GENE THERAPY MARKET: THERAPY TYPE FOOTPRINT       361

TABLE 587            GENE THERAPY MARKET: THERAPEUTIC AREA FOOTPRINT       362

TABLE 588            GENE THERAPY MARKET: ROUTE OF ADMINISTRATION FOOTPRINT 363

TABLE 589            GENE THERAPY MARKET: DETAILED LIST OF KEY STARTUPS/SMES    366

TABLE 590            GENE THERAPY MARKET: COMPETITIVE BENCHMARKING OF KEY STARTUPS/SMES          367

TABLE 591            GENE THERAPY MARKET: PRODUCT APPROVALS,

JANUARY 2022–DECEMBER 2024 370

TABLE 592            GENE THERAPY MARKET: DEALS, JANUARY 2022–DECEMBER 2024     371

TABLE 593            GENE THERAPY MARKET: EXPANSIONS, JANUARY 2022–DECEMBER 2024 373

TABLE 594            BIOGEN: COMPANY OVERVIEW 374

TABLE 595            BIOGEN: PRODUCTS OFFERED 375

TABLE 596            BIOGEN: DEALS, JANUARY 2022–DECEMBER 2024                 376

TABLE 597            NOVARTIS: COMPANY OVERVIEW            378

TABLE 598            NOVARTIS: PRODUCTS OFFERED             379

TABLE 599            NOVARTIS: DEALS, JANUARY 2022–DECEMBER 2024        380

TABLE 600            NOVARTIS: EXPANSIONS, JANUARY 2022–DECEMBER 2024                380

TABLE 601            NOVARTIS: OTHER DEVELOPMENTS, JANUARY 2022–DECEMBER 2024     381

TABLE 602            ALNYLAM PHARMACEUTICALS: COMPANY OVERVIEW          382

TABLE 603            ALNYLAM PHARMACEUTICALS: PRODUCTS OFFERED             383

TABLE 604            ALNYLAM PHARMACEUTICALS: PRODUCT APPROVALS,

JANUARY 2022–DECEMBER 2024 384

TABLE 605            ALNYLAM PHARMACEUTICALS: DEALS, JANUARY 2022–DECEMBER 2024 384

TABLE 606            ALNYLAM PHARMACEUTICALS: OTHER DEVELOPMENTS,

JANUARY 2022–DECEMBER 2024               385

TABLE 607            SAREPTA THERAPEUTICS: COMPANY OVERVIEW          386

TABLE 608            SAREPTA THERAPEUTICS: PRODUCTS OFFERED             387

TABLE 609            SAREPTA THERAPEUTICS: PRODUCT APPROVALS,

JANUARY 2022–DECEMBER 2024 388

TABLE 610            SAREPTA THERAPEUTICS: DEALS, JANUARY 2022–DECEMBER 2024     388

TABLE 611            JAZZ PHARMACEUTICALS: COMPANY OVERVIEW          390

TABLE 612            JAZZ PHARMACEUTICALS: PRODUCTS OFFERED             391

TABLE 613            JAZZ PHARMACEUTICALS: EXPANSIONS, JANUARY 2022–DECEMBER 2024 392

TABLE 614            FERRING: COMPANY OVERVIEW               393

TABLE 615            FERRING: PRODUCTS OFFERED                394

TABLE 616            FERRING: PRODUCT APPROVALS, JANUARY 2022–DECEMBER 2024     394

TABLE 617            FERRING: DEALS, JANUARY 2022–DECEMBER 2024        394

TABLE 618            FERRING: EXPANSIONS, JANUARY 2022–DECEMBER 2024                395

TABLE 619            PFIZER: COMPANY OVERVIEW  396

TABLE 620            PFIZER: PRODUCTS OFFERED   397

TABLE 621            PFIZER: PRODUCT APPROVALS, JANUARY 2022–DECEMBER 2024                398

TABLE 622            PFIZER: DEALS, JANUARY 2022–DECEMBER 2024                 398

TABLE 623            AMGEN: COMPANY OVERVIEW 399

TABLE 624            AMGEN: PRODUCTS OFFERED  400

TABLE 625            AMGEN: DEALS, JANUARY 2022–DECEMBER 2024                 400

TABLE 626            AMGEN: EXPANSIONS, JANUARY 2022–DECEMBER 2024                400

TABLE 627            JOHNSON & JOHNSON SERVICES: COMPANY OVERVIEW          401

TABLE 628            JOHNSON & JOHNSON SERVICES: PRODUCTS OFFERED             402

TABLE 629            JOHNSON & JOHNSON SERVICES: DEALS, JANUARY 2022–DECEMBER 2024 402

TABLE 630            JOHNSON & JOHNSON SERVICES: OTHER DEVELOPMENTS, JANUARY 2022–DECEMBER 2024            403

TABLE 631            DAIICHI SANKYO COMPANY: COMPANY OVERVIEW          404

TABLE 632            DAIICHI SANKYO COMPANY: PRODUCTS OFFERED             405

TABLE 633            BIOMARIN PHARMACEUTICAL: COMPANY OVERVIEW          406

TABLE 634            BIOMARIN PHARMACEUTICAL: PRODUCTS OFFERED             407

TABLE 635            BIOMARIN PHARMACEUTICAL: PRODUCT APPROVALS,

JANUARY 2022–DECEMBER 2024 407

TABLE 636            BIOMARIN PHARMACEUTICAL: EXPANSIONS, JANUARY 2022–DECEMBER 2024 408

TABLE 637            KYOWA KIRIN: COMPANY OVERVIEW    409

TABLE 638            KYOWA KIRIN: PRODUCTS OFFERED     410

TABLE 639            KYOWA KIRIN: PRODUCT APPROVALS, JANUARY 2022–DECEMBER 2024 411

TABLE 640            KYOWA KIRIN: DEALS, JANUARY 2022–DECEMBER 2024                411

TABLE 641            NIPPON SHINYAKU: COMPANY OVERVIEW                 412

TABLE 642            NIPPON SHINYAKU: PRODUCTS OFFERED                 413

TABLE 643            NIPPON SHINYAKU: DEALS, JANUARY 2022–DECEMBER 2024                414

TABLE 644            PTC THERAPEUTICS: COMPANY OVERVIEW                 415

TABLE 645            PTC THERAPEUTICS: PRODUCTS OFFERED                 416

TABLE 646            PTC THERAPEUTICS: PRODUCT APPROVALS, JANUARY 2022–DECEMBER 2024 416

TABLE 647            UNIQURE: COMPANY OVERVIEW              417

TABLE 648            UNIQURE: PRODUCTS OFFERED               418

TABLE 649            UNIQURE: DEALS, JANUARY 2022–DECEMBER 2024        418

TABLE 650            JUVENTAS CELL THERAPY: COMPANY OVERVIEW          419

TABLE 651            CRISPR THERAPEUTICS: COMPANY OVERVIEW                 419

TABLE 652            BLUEBIRD BIO: COMPANY OVERVIEW   420

TABLE 653            KRYSTAL BIOTECH: COMPANY OVERVIEW                 421

TABLE 654            SHANGHAI SUNWAY BIOTECH: COMPANY OVERVIEW          421

TABLE 655            JW (CAYMAN) THERAPEUTICS: COMPANY OVERVIEW          422

TABLE 656            IASO BIOTECHNOLOGY: COMPANY OVERVIEW                 422

TABLE 657            CARSGEN THERAPEUTICS HOLDINGS LIMITED: COMPANY OVERVIEW   423

TABLE 658            ADAPTIMMUNE: COMPANY OVERVIEW 423

TABLE 659            SIBIONO GENETECH CO. LTD.: COMPANY OVERVIEW          424

TABLE 660            ULTRAGENYX PHARMACEUTICAL INC.: COMPANY OVERVIEW   424

LIST OF FIGURES

FIGURE 1              GENE THERAPY MARKET SEGMENTATION & REGIONAL SCOPE            42

FIGURE 2              GENE THERAPY MARKET: YEARS CONSIDERED                 44

FIGURE 3              RESEARCH DESIGN         46

FIGURE 4              BREAKDOWN OF PRIMARY INTERVIEWS: GENE THERAPY MARKET          49

FIGURE 5              GENE THERAPY MARKET SIZE ESTIMATION (SUPPLY-SIDE ANALYSIS), 2023  51

FIGURE 6              MARKET SIZE ESTIMATION: APPROACH 1 (COMPANY REVENUE

ANALYSIS-BASED ESTIMATION), 2023     52

FIGURE 7              ILLUSTRATIVE EXAMPLE OF NOVARTIS AG: REVENUE SHARE ANALYSIS (2023)            52

FIGURE 8              MARKET SIZE ESTIMATION METHODOLOGY: TOP-DOWN APPROACH                53

FIGURE 9              GENE THERAPY MARKET: CAGR PROJECTIONS                 55

FIGURE 10            DATA TRIANGULATION METHODOLOGY                 57

FIGURE 11            GENE THERAPY MARKET, BY THERAPY TYPE, 2024 VS. 2032 (USD MILLION)      59

FIGURE 12            GENE THERAPY MARKET, BY VECTOR, 2024 VS. 2032 (USD MILLION)       60

FIGURE 13            GENE THERAPY MARKET, BY GENE TYPE, 2024 VS. 2032 (USD MILLION)                60

FIGURE 14            GENE THERAPY MARKET, BY THERAPEUTIC AREA, 2024 VS. 2032 (USD MILLION)         61

FIGURE 15            GENE THERAPY MARKET, BY DELIVERY METHOD, 2024 VS. 2032 (USD MILLION) 61

FIGURE 16            GENE THERAPY MARKET, BY ROUTE OF ADMINISTRATION, 2024                 62

FIGURE 17            GENE THERAPY MARKET, BY END USER, 2024 VS. 2032 (USD MILLION)       62

FIGURE 18            GEOGRAPHICAL SNAPSHOT OF GENE THERAPY MARKET               63

FIGURE 19            INCREASING INVESTMENTS IN GENE THERAPY RESEARCH—A KEY FACTOR DRIVING GROWTH 64

FIGURE 20            GENE SILENCING THERAPY ACCOUNTED FOR LARGEST SHARE OF

NORTH AMERICAN MARKET IN 2024       65

FIGURE 21            HOSPITALS TO DOMINATE END-USER MARKET TILL 2032              66

FIGURE 22            GERMANY TO REGISTER HIGHEST GROWTH DURING FORECAST PERIOD       66

FIGURE 23            GENE THERAPY MARKET: DRIVERS, RESTRAINTS, OPPORTUNITIES, AND CHALLENGES         67

FIGURE 24            GENE THERAPY MARKET: VALUE CHAIN ANALYSIS            80

FIGURE 25            GENE THERAPY MARKET: SUPPLY CHAIN ANALYSIS            82

FIGURE 26            GENE THERAPY MARKET: ECOSYSTEM 82

FIGURE 27            PATENT ANALYSIS FOR GENE THERAPY MARKET,

JANUARY 2014–DECEMBER 2024 86

FIGURE 28            AVERAGE SELLING PRICE TREND OF GENE THERAPIES,

BY TYPE, 2022–2024 (USD)            96

FIGURE 29            AVERAGE SELLING PRICE OF GENE THERAPIES, BY REGION, 2023 (USD) 98

FIGURE 30            TRENDS/DISRUPTIONS IMPACTING CUSTOMERS’ BUSINESSES           99

FIGURE 31            GENE THERAPY MARKET: PORTER’S FIVE FORCES ANALYSIS           101

FIGURE 32            INFLUENCE OF STAKEHOLDERS ON BUYING PROCESS OF GENE THERAPY PRODUCTS, BY DELIVERY METHOD             102

FIGURE 33            KEY BUYING CRITERIA FOR GENE THERAPY PRODUCTS, BY END USER            104

FIGURE 34            GENE THERAPY MARKET: INVESTMENT & FUNDING SCENARIO      105

FIGURE 35            NORTH AMERICA: GENE THERAPY MARKET SNAPSHOT          227

FIGURE 36            NIH FUNDING, 2014–2024               231

FIGURE 37            EUROPE: GENE THERAPY MARKET SNAPSHOT                 241

FIGURE 38            REVENUE ANALYSIS OF KEY PLAYERS, 2021–2023 (USD MILLION) 354

FIGURE 39            MARKET SHARE ANALYSIS OF KEY PLAYERS (2023)    355

FIGURE 40            GENE THERAPY MARKET: COMPANY EVALUATION MATRIX (KEY PLAYERS), 2023         358

FIGURE 41            GENE THERAPY MARKET: COMPANY FOOTPRINT       359

FIGURE 42            GENE THERAPY MARKET: COMPANY EVALUATION MATRIX

(STARTUPS/SMES), 2023                365

FIGURE 43            EV/EBITDA OF KEY VENDORS   368

FIGURE 44            YEAR-TO-DATE (YTD) PRICE TOTAL RETURN AND 5-YEAR STOCK BETA OF KEY VENDORS      368

FIGURE 45            GENE THERAPY MARKET: BRAND/PRODUCT COMPARATIVE ANALYSIS            369

FIGURE 46            BIOGEN: COMPANY SNAPSHOT (2023)   375

FIGURE 47            NOVARTIS: COMPANY SNAPSHOT (2023)                 379

FIGURE 48            ALNYLAM PHARMACEUTICALS: COMPANY SNAPSHOT (2023)             383

FIGURE 49            SAREPTA THERAPEUTICS: COMPANY SNAPSHOT (2023)             387

FIGURE 50            JAZZ PHARMACEUTICALS: COMPANY SNAPSHOT (2023)             391

FIGURE 51            FERRING: COMPANY SNAPSHOT (2023) 393

FIGURE 52            PFIZER: COMPANY SNAPSHOT (2023)      397

FIGURE 53            AMGEN: COMPANY SNAPSHOT (2023)    399

FIGURE 54            JOHNSON & JOHNSON SERVICES: COMPANY SNAPSHOT (2023)             402

FIGURE 55            DAIICHI SANKYO COMPANY: COMPANY SNAPSHOT (2023)             405

FIGURE 56            BIOMARIN PHARMACEUTICAL: COMPANY SNAPSHOT (2023)             406

FIGURE 57            KYOWA KIRIN: COMPANY SNAPSHOT (2023)                 410

FIGURE 58            NIPPON SHINYAKU: COMPANY SNAPSHOT (2023)    413

FIGURE 59            PTC THERAPEUTICS: COMPANY SNAPSHOT (2023)    415

FIGURE 60            UNIQURE: COMPANY SNAPSHOT (2023)                 417